Stop Sanfilippo Fundacion

Stop Sanfilippo Fundacion is an independent non-profit foundation based in Madrid, Spain. Established in 2012, the foundation is dedicated to the encouragement of Sanfilippo Syndrome research and development. The mission of Stop Sanfilippo is to encourage Sanfilippo Syndrome research to find a cure or a treatment, improve the quality of life of the affected children and their families, and spread knowledge about the illness to help achieve early diagnoses. The foundation is a registered member of Federación Española de Enfermedades Raras (FEDER), Organización Europea de Enfermedades Raras (EURORDIS), and Asociación Española de Fundaciones (AEF). The assets of the foundationmore

1 past transactions

Abeona Therapeutics

Grant in 2017
Abeona Therapeutics is developing gene therapy-based potential cures for the deadly childhood diseases Sanfilippo (SF) Syndrome Type A and Type B. Its multi-platform expertise across the manufacture, delivery, development, and discovery of the novel gene and cell therapies has it uniquely positioned for success. Underpinning the Company’s robust pipeline is its fully-operational manufacturing facility producing therapies and vectors for preclinical and clinical studies. Abeona is also developing the AIM Vector Platform: 100+ next-generation AAV capsids for delivering gene therapies targeting a wide range of organs and multiple routes of delivery.
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