Myonexus Therapeutics is a clinical-stage company focused on developing gene therapies for rare diseases, specifically targeting Limb-girdle muscular dystrophy (LGMD) Types 2D, 2B, 2E, 2L, and 2C. The company's innovative treatments are based on research conducted at Nationwide Children’s Hospital, which is recognized for its leadership in muscular dystrophy gene therapy discovery and translational research. In addition to LGMD, Myonexus is also engaged in developing therapies for other conditions, including Charcot-Marie-Tooth disease and various CNS-related disorders, utilizing advancements in precision genetic medicine to address unmet medical needs in these areas.
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