SmartPharm Therapeutics

SmartPharm Therapeutics is a development-stage biopharmaceutical company focused on creating non-viral gene therapies for serious and rare diseases. Founded in 2017 and based in Cambridge, Massachusetts, SmartPharm aims to develop a pipeline of gene-encoded therapeutics that allow patients' bodies to produce essential biologics for conditions requiring such treatments, including enzyme replacement and tissue restoration. The company's innovative platform emphasizes minimal immunogenicity, re-dosability for patients, and scalable manufacturing, while also seeking to simplify regulatory processes. By leveraging insights gained from previous gene therapy developments, SmartPharm integrates advanced technologies to produce optimal gene-encoded therapies, thereby enhancing the therapeutic benefits for patients without the complications associated with viral vectors.